FDA Approves First Gene Therapy Offering New Hope for Sickle Cell Disease
The U.S. Food and Drug Administration has approved a landmark gene therapy for sickle cell disease, marking a major advance in the treatment of a painful inherited blood disorder that affects hundreds of thousands of people worldwide.How the therapy worksDeveloped by CRISPR Therapeutics and Vertex Pharmaceuticals, the treatment uses a patient’s own blood stem cells, which are modified outside the body to help…
Bilim 65 görüntülenme 136g önce